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Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy
Nathalie Cartier et al. · Science
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5 Nov 2009 |
1,526 |
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Large-Scale Manufacture and Characterization of a Lentiviral Vector Produced for Clinical Ex Vivo Gene Therapy Application
Otto-Wilhelm Merten, Sabine Charrier, Nicolas Laroudie et al. · Human Gene Therapy
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2 Nov 2010 |
185 |
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Determination of Anti-Adeno-Associated Virus Vector Neutralizing Antibody Titer with an In Vitro Reporter System
Amine Meliani, Christian Leborgne, Sabrina Triffault et al. · Human Gene Therapy Methods
Open access |
29 Mar 2015 |
115 |
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Strategy to detect pre-existing immunity to AAV gene therapy
Lillian Falese, Krystal Sandza, Bridget Yates et al. · Gene Therapy
Open access |
6 Nov 2017 |
100 |
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A phase I trial of adeno-associated virus serotype 1-γ-sarcoglycan gene therapy for limb girdle muscular dystrophy type 2C
S. Herson et al. · Brain
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10 Jan 2011 |
90 |
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Gene transfer vector biodistribution: pivotal safety studies in clinical gene therapy development
Patrick Gonin, Claire Rogel-Gaillard · Gene Therapy
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29 Sep 2004 |
71 |
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Major Subsets of Human Dendritic Cells Are Efficiently Transduced by Self-Complementary Adeno-Associated Virus Vectors 1 and 2
Philippe Véron, Valérie Allo, Christel Rivière et al. · Journal of Virology
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22 Feb 2007 |
53 |
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Non-clinical Safety and Efficacy of an AAV2/8 Vector Administered Intravenously for Treatment of Mucopolysaccharidosis Type VI
Rita Ferla, Marialuisa Alliegro, Jean‐Brice Marteau et al. · Molecular Therapy — Methods & Clinical Development
Open access |
24 Jul 2017 |
51 |
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Real-time quantitative PCR for the design of lentiviral vector analytical assays
Christophe Delenda, Claire Rogel-Gaillard · Gene Therapy
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Oct 2005 |
46 |
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Computerized cardiotocography analysis during labor – A state‐of‐the‐art review
Imane Ben M’Barek, Grégoire Jauvion, Pierre‐François Ceccaldi · Acta Obstetricia Et Gynecologica Scandinavica
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20 Dec 2022 |
33 |
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RSV N-nanorings fused to palivizumab-targeted neutralizing epitope as a nanoparticle RSV vaccine
Pierre‐Louis Hervé, Charlotte Deloizy, Delphyne Descamps et al. · Nanomedicine Nanotechnology Biology and Medicine
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23 Aug 2016 |
32 |
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Liver-Directed Adeno-Associated Virus–Mediated Gene Therapy for Mucopolysaccharidosis Type VI
Nicola Brunetti‐Pierri et al. · NEJM Evidence
Open access |
6 Jun 2022 |
27 |
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Efficacy, pharmacokinetics, and safety in the mouse and primate retina of dual AAV vectors for Usher syndrome type 1B
Rita Ferla et al. · Molecular Therapy — Methods & Clinical Development
Open access |
10 Feb 2023 |
25 |
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The anti-influenza M2e antibody response is promoted by XCR1 targeting in pig skin
Charlotte Deloizy, Even Fossum, Christophe Barnier-Quer et al. · Scientific Reports
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3 Aug 2017 |
20 |
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Preclinical Evaluation of a Cell-Based Gene Therapy Using the Sleeping Beauty Transposon System in Choroidal Neovascularization
Maria Angeles Rodriguez Hernandez, Sergio Recalde, Laura García‐García et al. · Molecular Therapy — Methods & Clinical Development
Open access |
8 Nov 2019 |
18 |
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Osteopontin in the host response to Leishmania amazonensis
Émilie Giraud, Eline Rouault, Laurence Fiette et al. · BMC Microbiology
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8 Feb 2019 |
14 |
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rAAV Vector Product Characterization and Stability Studies
Richard O. Snyder, Muriel Audit, Joyce D. Francis · Methods in molecular biology
Book chapter |
27 Sep 2011 |
13 |
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Efficient transduction of monocyte‐ and CD34+‐ derived Langerhans cells with lentiviral vectors in the absence of phenotypic and functional maturation
Philippe Véron, Sylvie Boutin, Jacky Bernard et al. · The Journal of Gene Medicine
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2 Jun 2006 |
12 |
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Confirmatory detection of neutralizing antibodies to AAV gene therapy using a cell-based transduction inhibition assay
Theresa Kasprzyk, Sabrina Triffault, Brian R. Long et al. · Molecular Therapy — Methods & Clinical Development
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7 Jan 2022 |
8 |
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2017-2023: state of the art of gene therapies in rare diseases in Europe: the dynamics of clinical R&D, new approved treatments and expected therapies in the pipelines
Tristan Gicquel, Lucas Cortial, Karyna Lutsyk et al. · Rare Disease and Orphan Drugs Journal
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3 Nov 2023 |
5 |
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“RCL-Pooling Assay”: A Simplified Method for the Detection of Replication-Competent Lentiviruses in Vector Batches Using Sequential Pooling
Guillaume Corre, Michel Dessainte, Jean‐Brice Marteau et al. · Human Gene Therapy
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22 Jan 2016 |
5 |
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Assessment of Therapeutic Potential of A Dual Aav Approach for Duchenne Muscular Dystrophy
Sonia Albini, Laura Palmieri, Auriane Dubois et al. · Preprints.org
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29 Jun 2023 |
4 |
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468. GLP-Compliant Non-Clinical Safety and Biodistribution of a Recombinant AAV2/8 Vector Administered Intravenously for Treatment of Mucopolysaccharidosis Type VI
Rita Ferla, Jean‐Brice Marteau, Séverine Pouillot et al. · Molecular Therapy
Open access |
May 2016 |
2 |
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Enhanced Lentiviral Transduction of Monocyte-Derived Dendritic Cells in The Presence of Conditioned Medium from Dying Monocytes
Carole Masurier, Sylvie Boutin, Philippe Véron et al. · Human Gene Therapy
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Feb 2007 |
2 |
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Transposon-Based, Targeted Ex Vivo Gene Therapy to Treat Age-Related Macular Degeneration (TargetAMD)
Gabriele Thumann, Maria Perdikomati-Dahmen, Susanne Binder et al. · Human Gene Therapy Clinical Development
Open access |
Jun 2015 |
1 |
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Tête de perçage à vibrations axiales
George Moraru, Philippe Véron, Patrice Rabaté · SAM, the Arts et Métiers ParisTech open access repository (Paris Institute of Technology)
Open access |
2010 |
0 |
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Results of a biodistribution study of Venus transfected pigment epithelial cells transplanted subretinally in rabbits
Martina Kropp, Argyrios Chronopoulos, Alain Conti et al. · Investigative Ophthalmology & Visual Science
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26 Sep 2016 |
0 |
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464. RCL-Pooling Assay: A Simplified Method for the Detection of Replication Competent Lentiviruses in Vector Batches Using Sequential Pooling
Guillaume Corre, Michel Dessainte, Jean‐Brice Marteau et al. · Molecular Therapy
Open access |
May 2016 |
0 |