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Treatment of Fabry’s Disease with the Pharmacologic Chaperone Migalastat
Dominique Paul Germain et al. · New England Journal of Medicine
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10 Aug 2016 |
566 |
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Oral pharmacological chaperone migalastat compared with enzyme replacement therapy in Fabry disease: 18-month results from the randomised phase III ATTRACT study
Derralynn A. Hughes et al. · Journal of Medical Genetics
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10 Nov 2016 |
395 |
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Long-term efficacy and safety of migalastat treatment in Fabry disease: 30-month results from the open-label extension of the randomized, phase 3 ATTRACT study
Ulla Feldt‐Rasmussen, Derralynn A. Hughes, Gere Sunder–Plassmann et al. · Molecular Genetics and Metabolism
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15 Aug 2020 |
81 |
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Safety and efficacy of alternative alglucosidase alfa regimens in Pompe disease
Laura E. Case, Carl Bjartmar, Claire L Morgan et al. · Neuromuscular Disorders
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20 Dec 2014 |
59 |
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Head-to-head trial of pegunigalsidase alfa versus agalsidase beta in patients with Fabry disease and deteriorating renal function: results from the 2-year randomised phase III BALANCE study
Eric L Wallace et al. · Journal of Medical Genetics
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8 Nov 2023 |
49 |
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Reduction of Plasma Globotriaosylsphingosine Levels After Switching from Agalsidase Alfa to Agalsidase Beta as Enzyme Replacement Therapy for Fabry Disease
Özlem Göker-Alpan, Michael J. Gambello, Gustavo H. B. Maegawa et al. · JIMD Reports
Book chapterOpen access |
2015 |
30 |
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Effect and Tolerability of Agalsidase Alfa in Patients with Fabry Disease Who Were Treatment Naïve or Formerly Treated with Agalsidase Beta or Agalsidase Alfa
Özlem Göker-Alpan, Khan J. Nedd, Suma P. Shankar et al. · JIMD Reports
Book chapterOpen access |
2015 |
18 |
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Altered immune phenotypes in subjects with Fabry disease and responses to switching from agalsidase alfa to agalsidase beta.
Renuka Pudi Limgala, Tabitha Jennelle, Matthew L. Plassmeyer et al. · PubMed
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2019 |
16 |
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Targeting Job Retention Services for Welfare Recipients
Anu Rangarajan, Peter Z. Schochet, Dexter Chu
Book chapterOpen access |
Sep 2002 |
9 |
| 10 |
Once every 4 weeks - 2 mg/kg of pegunigalsidase alfa for treating Fabry disease Preliminary results of a phase 3 study
Myrl D. Holida, John A. Bernat, Nicola Longo et al. · Molecular Genetics and Metabolism
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Feb 2019 |
8 |
| 11 |
Impact of Infliximab-dyyb (Infliximab Biosimilar) on Clinical and Patient-Reported Outcomes: 1-Year Follow-up Results from an Observational Real-World Study Among Patients with Inflammatory Bowel Disease in the US and Canada (the ONWARD Study)
Bincy P Abraham, Bertus Eksteen, Khan J. Nedd et al. · Advances in Therapy
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16 Mar 2022 |
7 |
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eP149: Safety and efficacy of pegunigalsidase alfa, every 4 weeks, in Fabry disease: Results from the phase 3, open-label, BRIGHT study
John A. Bernat, Myrl D. Holida, Nicola Longo et al. · Genetics in Medicine
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Mar 2022 |
7 |
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Evaluating Changes in del Nido Cardioplegia Practices in Adult Cardiac Surgery
Donald S. Likosky, Xiaoting Wu, David C Fitzgerald et al. · Journal of ExtraCorporeal Technology
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Sep 2020 |
6 |
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Compartment Syndrome of the Hand Secondary to Intravenous Extravasation.
Cara M Barber, Matthew P. Fahrenkopf, Nicholas S. Adams et al. · PubMed
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2018 |
3 |
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Embedding IP Unique Shortest Path Topology on a Wavelength-Routed Network: Normal and Survivable Design
Gaurav Agrawal, Deep Medhi · IEEE/ACM Transactions on Networking
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20 Apr 2015 |
3 |
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P-545. Feasibility, Fidelity, and Effectiveness of Administering CABENUVA in Infusion Centers
Cassidy A. Gutner, Conn M. Harrington, Gilda Bontempo et al. · Open Forum Infectious Diseases
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29 Jan 2025 |
2 |
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Analysis of the baseline characteristics of Fabry disease patients screened for the pegunigalsidase alfa phase III BALANCE study
David G. Warnock et al. · Molecular Genetics and Metabolism
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Feb 2019 |
2 |
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A Phase 4 Study to Evaluate the Safety and Tolerability of Higher Infusion Rates of Agalsidase Beta to Shorten Infusion Duration in Fabry Disease: Interim Analysis
Maryam Banikazemi, Özlem Göker-Alpan, Khan J. Nedd et al. · Journal of the American Society of Nephrology
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Oct 2024 |
1 |
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Feasibility, Fidelity, and Effectiveness of Administering Long-Acting Cabotegravir + Rilpivirine in Infusion Centers in the United States: Findings From the Phase 4 GLACIER Implementation Study
Cassidy A. Gutner, Conn Harrington, Gilda Bontempo et al. · Journal of the International Association of Providers of AIDS Care (JIAPAC)
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2026 |
0 |
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Additional file 1 of Explaining the Diffusion of Project ECHO
James W. Dearing, R. Sam Larson · Figshare
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2025 |
0 |
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Additional file 1 of Explaining the Diffusion of Project ECHO
Dearing, James W., Larson, R. Sam · Figshare
Open access |
2025 |
0 |
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#197 A phase 4 study to evaluate the safety and tolerability of higher infusion rates of agalsidase beta to shorten the infusion duration in Fabry disease—Preliminary data
Maryam Banikazemi, Özlem Göker-Alpan, Khan J. Nedd et al. · Nephrology Dialysis Transplantation
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Oct 2025 |
0 |
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P236: Extending the interval between pegunigalsidase alfa infusions in patients with Fabry disease: Five-year interim results from the ongoing BRIGHT51 study
John A. Bernat et al. · Genetics in Medicine Open
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2025 |
0 |
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Prevalence of frailty in the elderly with rheumatoid arthritis
Rodrigo Lozano-Lozano, David Vega‐Morales, Macarena del Rosario Sifuentes-Martinez et al. · The Journal of Latin American geriatric medicine
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5 Mar 2025 |
0 |
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P511 Baseline characteristics of ulcerative colitis patients in the vedolizumab PASS study: a cohort study assessing the safety and effectiveness of vedolizumab compared to other biologic agents (01)
Douglas C. Wolf et al. · Journal of Crohn s and Colitis
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26 Jan 2017 |
0 |
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Comparison of clinical practice guidelines and actual clinical practice in Fabry disease diagnosis
Dawn A. Laney, Amy L White, Myrl D. Holida et al. · Molecular Genetics and Metabolism
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27 Jan 2015 |
0 |
| 27 |
Evaluation of glycosphingolipid clearance in patients with Fabry disease treated with agalsidase alfa who switched to agalsidase beta (the INFORM study)
John A. Barranger, Michael J. Gambello, Özlem Göker-Alpan et al. · Molecular Genetics and Metabolism
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27 Jan 2014 |
0 |
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HGT-REP-059 treatment protocol: effect and tolerability of open-label agalsidase alfa in patients with Fabry disease
Özlem Göker-Alpan, Khan J. Nedd, Suma P. Shankar et al. · Molecular Genetics and Metabolism
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27 Jan 2014 |
0 |
| 29 |
Anti-drug antibody findings of agalsidase alfa for Fabry Disease: Treatment-naïve or formerly treated with agalsidase beta
Özlem Göker-Alpan, Khan J. Nedd, Suma P. Shankar · Molecular Genetics and Metabolism
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26 Jan 2013 |
0 |